Gene therapies have made spectacular progress in delivering new cures for previously intractable disease, where virus ve...
Advancement in Metabolic dysfunction-Associated SteatoHepatitis (MASH) treatment: the first FDA approved drug
The FDA approves Madrigal Pharmaceuticals’ Rezdiffra for Metabolic dysfunction-Associated SteatoHepatitis (MASH), ...
Unprecedented blood biomarker enables ALS drug approval
Biogen’s Qalsody (tofersen) has been approved by the US Food and Drug Administration (FDA) for treating a rare form of...
First amniotic fluid-derived human organoids will advance prenatal precision medicine in a new era.
Researchers created 3D models of developing organs from fetal cells, which are present in amniotic fluid, to help prenat...
Immunotherapy and cell-based immunotherapy: TILs on stage
CAR-T therapy is one of the most revolutionary approaches of these years, but Tumor-infiltrating lymphocytes (TILs) are...
Breaking barriers: a blood test to study gene expression in the brain
The released markers of activity (RMAs) is a non-invasive monitoring of gene expression in the brain with a simple blood...