Take home message Targeting poison exons can restore protein abundance and ameliorate the outcomes of genetic disorders ...
Vitamin B2: potential driver for cancer therapy
Cancer treatment has come a long way, but many therapies still struggle with targeting tumor cells without damaging heal...
Echoes of hope: DB-OTO gene therapy pioneers genetic hearing loss treatment DB-OTO Gene therapy: advancing treatment for genetic hearing loss
Regeneron Pharmaceuticals’ gene therapy, DB-OTO, has shown promising initial results in improving hearing for chil...
The Future of Weight Loss: What Will Be Next After Wegovy?
The next generation of weight loss treatments promises to be more effective, convenient, and accessible, building on the...
New Horizons in Type 1 Diabetes: FDA Approval of Lantidra and Emerging Therapies
The FDA has approved Lantidra, a groundbreaking donor-derived pancreatic islet cell therapy for type 1 diabetes, providi...
Why gene therapies must go virus-free
Gene therapies have made spectacular progress in delivering new cures for previously intractable disease, where virus ve...